Two Wisconsin sisters are among the first to get gene therapy for genetic deafness
At Children's Wisconsin, 3-year-old Cleo and her sister Lennon had FDA-approved gene therapy surgery in July. They are responding to sounds such as a bark and their mother's humming. Results vary, and durability is unknown.
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At Children's Wisconsin, 3-year-old Cleo and her sister Lennon had gene therapy surgery in July for genetic deafness. The therapy is FDA-approved, and the sisters are among the first children in the United States to receive it for this purpose. They are now responding to sounds, including a dog's bark and their mother humming.
That is what their family is seeing. It is not a result that every child will have. How long the change lasts is not yet known, and the report does not say the sisters now hear the way a typical ear does.
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